Zevra Therapeutics

April Fools’ may be for jokes, but rare disease is no laughing matter. At Zevra, we’re committed to advancing life-changing therapies and raising awareness for patients and families living with rare diseases. #RareDisease #Awareness

Help advance science in VEDS. The DiSCOVER Trial for celiprolol is enrolling now. Learn more: discoverceliprolol.com #VEDS #RareDisease

We’re heading to #ACMGMtg26! Join us in Baltimore, MD as we present a poster on the various NPC1 genotypes in Niemann-Pick disease type C patients on Fri, Mar 13 at 10:30 a.m. ET and host booth #2008 throughout the meeting. Stop by to meet our team & learn more about our work.

We’re proud to partner with @GeneDx to launch a Sponsored Genetic Testing Program for eligible patients in the U.S. with suspected Niemann-Pick disease type C (NPC). Read the press release: businesswire.com/news/home/2026… #RareDisease #NPC #GeneticTesting

$ZVRA reports fourth quarter and full year 2025 financial results and provides a corporate update. Join our LIVE webcast TODAY at 4:30 p.m. ET: bit.ly/3OXgtr0 For more, find the full release here: bit.ly/3N9An1q #RareDiseases #InvestorRelations #IR

Our President and CEO Neil McFarlane will share the latest company updates in a fireside chat at the Citizens 2026 Life Sciences Conference on Wednesday, March 11, 2026 at 9:00 am ET. Register for the webcast presentation here: bit.ly/4rSfHcM

We’re pleased to welcome Justin Renz as Zevra’s new Chief Financial Officer. With 25+ years of biopharma finance leadership, Justin brings strong experience and operational insight. Read the release: investors.zevra.com/news-releases/…

Our President & CEO Neil McFarlane attended the inaugural CNBC Cures Summit to advance solutions accelerating rare disease innovation. The call to remove barriers & drive meaningful change aligns with Zevra’s commitment to the rare disease community. #RareDisease #CNBCCures

$ZVRA will report fourth quarter and full year 2025 financial results and provide a corporate update on Monday, March 9, 2026, with a live webcast at 4:30 p.m. ET. For registration details, see the release: bit.ly/40Af1NI #RareDiseases #InvestorRelations #IR

Today is Rare Disease Day. At Zevra, our commitment to education, understanding, and the rare disease community continues all year long. Learn how you can get involved at #community-support" target="_blank" rel="nofollow noopener">learnnpc.com/npc-symptoms/#… #ShowYourStripes #RareDiseaseDay #RareDisease

The Zevra team at last week’s Firefly Dreams Gala! A powerful evening supporting research & education for Niemann-Pick disease type C (NPC). This year’s cowboy chic theme made it unforgettable, but the mission is what truly matters. #RareDisease #NPC #FireflyDreams

Did you know? Niemann-Pick disease type C is inherited in an autosomal recessive pattern, meaning both parents must carry a copy of the affected gene for a child to develop the condition. Learn more about NPC and the path to diagnosis at learnnpc.com/diagnosis-and-… #RareDisease

Did you know? NPC symptoms can vary widely from person to person and because they can overlap with other conditions, there may be delays in diagnosis. Increased awareness can help: learnnpc.com/npc-symptoms/ #RareDisease

Did you know? Niemann-Pick disease type C (NPC) is a rare, inherited lysosomal storage disorder affecting people of all ages, and its variability often makes diagnosis challenging. Learn more at learnnpc.com #RareDisease

Honored to celebrate the day with the opening bell ceremony at @Nasdaq, what an incredible moment for our team!

We’re excited to ring the @Nasdaq opening bell! Watch via live stream as our CEO, Neil McFarlane delivers opening remarks: nasdaq.com/marketsite/bel…

Wrapping up an action-packed week at WORLDSymposium! It’s always so meaningful to connect with the rare disease community. Thank you to the organizers for another outstanding event. #WORLDSymposium2026 #RareDisease

Attending #WORLDSymposium? Don’t miss Zevra Therapeutics’ satellite symposium on Feb 5 at 12:15 pm PT. Zevra will also share data via podium and poster presentations. Read our press release to learn more investors.zevra.com/news-releases/… #WORLDSymposium2026

Attending the WORLDSymposium? Stop by and see us in person at booths #213 and #507. #WORLDSymposium #WORLDSymposium2026

February is Rare Disease Awareness Month, and we’re proud to stand with individuals and families impacted by rare diseases — including Niemann-Pick disease type C (NPC). Learn more at: zevra.com/niemann-pick-d… #RareDisease