پن کیا گیا ٹویٹ

Oh, what difference can trofinetide make??
2013 NNZ-2566 trial, 1/6 the current dose.
Day 30- 4 days off full meds, 2 days off all meds (I drew the flower)
Day 35 -9 days off full meds, 7 days off all meds
#RettSyndrome #Trofinetide #WaitingforMarch12


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