GENETHON France

📢[COMMUNIQUE DE PRESSE] @GenethonFr × @AmpersandBio Un partenariat exclusif pour concevoir des vecteurs AAV à très haute spécificité tissulaire, afin de renforcer la sécurité et l’efficacité des thérapies géniques. 👉urlr.me/AhbdXc #GeneTherapy #AAV #Innovation

📢[PRESS RELEASE] @GenethonFr × @AmpersandBio An exclusive partnership to engineer AAV vectors with very high tissue specificity, aiming to enhance the safety and efficacy of gene therapies. 👉 urlr.me/9B3dMJ #GeneTherapy #AAV #Innovation

[#ASGCT2026] – Oral presentations 📌Join us for @GenethonFr 's last talks at ASGCT 2026 with: Gérald Perret, Giuseppe Ronzitti and Paola Galbiati Advancing clinical gene therapy for rare diseases. @ASGCTherapy #GeneTherapy #ClinicalTrials

[#ASGCT2026] - Poster session 🤝👨‍🎓 👩‍🎓Meet Genethon scientists presenting: Estelle Creoff - Poster [ASGCT353] Adrian Westhaus - Poster [ASGCT1167] Isabelle Richard - Poster [ASGCT1489] Youssef Krimi Benchekroun - Poster [ASGCT1891] Rim Harb - Poster [ASGCT2476] @ASGCTherapy

[#ASGCT2026] – Oral presentation today, Isabelle Richard, PhD will share expert insights on: 🧬 Challenges and solutions in the development of gene therapy for muscular dystrophies A key session not to miss. @ASGCTherapy #GeneTherapy #MuscularDystrophy #DMD

🤝👨‍🎓 👩‍🎓[#ASGCT2026] - Poster session Meet our teams, discover @GenethonFr's work on genome editing, safety and preclinical models: Lydie Debaize - Poster [ASGCT1193] Jérôme Denard - Poster [ASGCT1220] Badih Salman - Poster [ASGCT870] @ASGCTherapy #geneediting #genetherapy

[#ASGCT2026] – Oral presentations today 📌Don’t miss oral presentations with Youssef Krimi Benchekroun, Louisa Jauze, Dr. Barry Byrne and Giulia Scalisi. @ASGCTherapy #GeneTherapy #RareDiseases

[#ASGCT2026] – Poster sessions 📌🤝Explore @GenethonFr's research in gene therapy and genome editing: Estelle Creoff - Poster [ASGCT355] Philippe Veron - Poster [ASGCT1186] Alexandra Tachtsidi - Poster [ASGCT1368] Rim Harb - Poster [ASGCT1830] Marion Derome - Poster [ASGCT1163]

📢 The 29th Annual #ASGCT2026 Congress kicks off today 11, in Boston, MA! @GenethonFr will present 21 scientific contributions: - 8 oral presentations - 13 posters! urlr.me/FYrAy4 Looking forward to sharing our latest advances in gene therapy! #GeneTherapy

🔬 Evaluating a single treatment across multiple diseases that share a common biological mechanism: a promising “basket” clinical trial approach to accelerate therapeutic innovation. 👉urls.fr/yjE3ki @Telethon_France @Inst_Myologie @IStemFrance #ClinicalTrials

🔬 Évaluer un même traitement dans plusieurs maladies partageant un mécanisme biologique commun: une approche prometteuse des essais cliniques "basket" pour accélérer l’innovation thérapeutique. 👉urlr.me/4eAqpC @Telethon_France @Inst_Myologie @IStemFrance # essais

#ASGCT2026 | Genethon at @ASGCTherapy Efficacy data from 3 gene therapy trials: pivotal GNT0004 (Duchenne), first clinical results of ATA200 (LGMD R5), and first‑in‑patient proof that imlifidase can overcome pre‑existing AAV immunity. 8 talks, 13 posters. urlr.me/t9qXkJ

⏰ Good morning fellow #CGMED26 attendees! Day 1 of the conference is underway. Don’t miss @GenethonFr's activities presentation by Imen Mestiri, PhD, Business Development Lead, April 29th at 3:45 pm. #GeneTherapy #RareDiseases #BusinessDevelopment #Genother

New study in Molecular Therapy: @GenethonFr uses #CRISPRCas9 to boost utrophin expression in #Duchenne muscular dystrophy. A mutation‑independent genome editing strategy with promising preclinical benefits. 👉urlr.me/GRYk8Q #GeneTherapy #GenomeEditing #DMD

Nouvelle étude dans Molecular Therapy : @GenethonFr utilise l’#éditiondugénome #CRISPRCas9 pour augmenter l’expression de l’utrophine dans la myopathie de #Duchenne. Une stratégie indépendante des mutations, prometteuse en préclinique. 👉urlr.me/U3faPe #DMD

🎉 100 548 314 € collectés pour le Téléthon 2025 ! Grâce à vous : donateurs, bénévoles, familles, partenaires, chercheurs, grâce à @jesuissanta999, aux artistes, animateurs et aux équipes de @Francetele, cette collecte est EXCEPTIONNELLE ! MERCI 💛 👉 afm-telethon.fr/fr/actualites/…

@GenethonFr at #SFTCG2026: 4 talks & 8 posters at @ICMParis advancing safe, effective gene therapies. AAV, CRISPR, new preclinical models, immune tolerance, rAAV manufacturing… Meet our teams! 📄 Full program: sftcg.fr/event-programme

@GenethonFr au #SFTCG2026 : 4 talks & 8 posters au @ICMParis pour faire avancer des thérapies géniques sûres et efficaces. AAV, CRISPR, nouveaux modèles précliniques, tolérance immunitaire, production de rAAV… Rencontrez nos équipes ! Programme: sftcg.fr/event-programme

@Genethon at #SFTCG2026: 4 talks & 8 posters at @ICMParis advancing safe, effective gene therapies. AAV, CRISPR, new preclinical models, immune tolerance, rAAV manufacturing… Meet our teams! 📄 Full program: sftcg.fr/event-programme

📢 Meet us at @AdTherapiesConf – March 17, 14:55 (Track 7) 🎤 Angela Columbano will share our latest innovations in gene therapy platforms. 🤝 Meet Angela & Imen Mestiri in London to explore partnerships shaping the future of advanced therapies. #GeneTherapy