PackGene Biotech

𝐀𝐀𝐕 𝐠𝐞𝐧𝐞 𝐭𝐡𝐞𝐫𝐚𝐩𝐲 𝐦𝐢𝐥𝐞𝐬𝐭𝐨𝐧𝐞 𝐢𝐧 𝐄𝐮𝐫𝐨𝐩𝐞. 𝐍𝐨𝐫𝐰𝐚𝐲 issued a reimbursement recommendation for 𝐇𝐄𝐌𝐆𝐄𝐍𝐈𝐗. 𝐅𝐨𝐥𝐥𝐨𝐰 𝐏𝐚𝐜𝐤𝐆𝐞𝐧𝐞 𝐨𝐧 𝐋𝐢𝐧𝐤𝐞𝐝𝐢𝐧 lnkd.in/e5GY5tAR & 𝐒𝐮𝐛𝐬𝐜𝐫𝐢𝐛𝐞 𝐭𝐨 𝐎𝐮𝐫 𝐍𝐞𝐰𝐬𝐥𝐞𝐭𝐭𝐞𝐫.

👏 Meet PackGene at #BSGCT2025 in London! 🗓️June 20 📍Royal Holloway University Let’s talk AAV, LVV, mRNA, & plasmid innovation with Xisha Huang. #GeneTherapy #Biotech #CDMO #PackGene

We’re heading to #EACR2025 in Lisbon! 📍Booth #17  🗓️ June 16–19 Explore our full-service #CRO and #CDMO offerings: 🧬 AAV | Lentivirus | Plasmid | mRNA & LNP Let’s talk cancer gene therapy innovation. 📩 heng.hu@packgene.com #GeneTherapy #CancerResearch #Biotech #PackGene

📢 Heading to #BIO2025 in Boston, June 16–19? Meet PackGene’s CSO, Dr. Xin Swanson, to talk #GeneTherapy innovation. 📍Booth 387 – great science and conversations. Let’s connect! #AAV #mRNA #Plasmid #CDMO #Biotech

We’re at #NVGCT2025 ⌛️June 10–11 in Lenteren, Netherland! Stop by the PackGene booth & meet Dr. Heng Hu to learn about our AAV, LVV, mRNA & plasmid platforms. packgene.com/event/nvgct-an… #GeneTherapy #Biotech #mRNA #AAV #PackGene

Conquering the Complexities of AAV Manufacturing: Advances in Efficiency, Scalability, Compliance GEN talked with several CDMOs and/or CROs about new ways they are addressing AAV manufacturing challenges. @PackGeneBiotech @CRiverLabs @LonzaGroup #AAV hubs.li/Q03prQ2j0

🚨 PackGene is heading to #AACR2025! 🎯 Visit us at Booth 4346 in Chicago, Apr 25–30 🧬 Discover how our AAV, lentiviral, and mRNA platforms are accelerating cancer research. 🎁 Stop by for a chat, insights, and free swag! 🎓 Academic promo: packgene.com/promotion/acad… #GeneTherapy

24-month data from Beacon Therapeutics' AGTC-501 HORIZON Trial for XLRP now in @AmerAcadOphth! Promising results in gene therapy. #GeneTherapy #RetinalDisease #XLRP #AAV #Packgene packgene.com/frontier/25031…

Arbor Biotechnologies closes $73.9M Series C to advance ABO-101 for Primary Hyperoxaluria Type 1 (PH1). This milestone highlights the potential of CRISPR Cas12i2 and signals continued investor confidence in groundbreaking therapies. #GeneEditing #CRISPR packgene.com/frontier/25031…

HUGE NEWS! Beam Therapeutics achieves FIRST-EVER clinical genetic correction in AATD trial!  BEAM-302 shows: ✅ ⬆️ AAT levels (exceeding therapeutic threshold!) ✅ ⬇️ 78% reduction in mutant Z-AAT! ✅ Corrected M-AAT production! ✅ Great safety profile! investors.beamtx.com/news-releases/…

Academic Discovery Engine Accelerate your research from design to delivery with academic-exclusive offers packgene.com/support/promot… #AAV #ViralVector #CRISPR #ResearchOptimization

🧬This #RareDiseaseDay, we’re breaking barriers in gene therapy! ✅Advancing SPG56 & OTOF hearing loss treatments 🔗No patient left behind. Learn more: packgene.com/event/rare-dis… #GeneTherapy #RareDiseases #BreakingBarriers #PackGene

Allogene ($ALLO) gets FDA IND clearance for ALLO-329, an allogeneic CAR T for autoimmune diseases. Phase1 trial starts mid-2025 for lupus, myopathies, & systemic sclerosis. Targets CD19+ B cells & CD70+ T cells. Dagger® tech may eliminate lymphodepletion. packgene.com/frontier/25013…

ELEVIDYS shows sustained benefits for 2 YEARS in ambulatory #DMD patients! Sarepta's EMBARK study delivers promising long-term data. ✨ packgene.com/frontier/25013… #RareDisease #GeneTherapy #AAV #Packgene #Sarepta

We’re at #PMWC2025! Visit PackGene at Booth A421 to discuss our GMP viral (AAV) and non-viral solutions. Let’s innovate together and shape the future of precision medicine. Booth A421—see you there! #GeneTherapy #AAV #PrecisionMedicine #Biotech

Vertex & Orna team up to develop gene therapies for SCD & TDT! $65M upfront to boost RNA-based innovations using Orna's LNP tech. This collab drives progress toward better rare disease treatments. packgene.com/frontier/25011… #GeneTherapy #SCD #VertexPharma

A Global Alliance to Save Lives: How Two Parents and PackGene Are Redefining What’s Possible in Gene Therapy with Help from Weill Cornell Medicine Read more👉packgene.com/news/250107/ Video link: youtube.com/watch?v=QwlYjW… #GeneTherapy

Novartis' OAV101 IT gene therapy shows promise for type II SMA patients aged 2-17! 🚀Favorable Phase III results could expand options for older pediatric patients. packgene.com/frontier/25010… #GeneTherapy #SMA #RareDisease

✨Medical Breakthroughs of 2024✨ · Enhertu & Tagrisso redefine cancer care · GLP-1 meds tackle obesity, heart disease, & sleep apnea · Lenacapavir: 100% HIV prevention · New treatments for Duchenne MD, schizophrenia & more packgene.com/frontier/20250… #GeneTherapy

GEMMABio raises $34M to advance #GeneTherapy for rare diseases! With strong partnerships and innovative approaches, they’re redefining treatment accessibility. packgene.com/frontier/24122… #HealthcareInnovation #RareDiseases