Patient Worthy

At Patient Worthy, we aim to publish the realities of #RareDisease. Your voice is integral to achieving that goal. Would you like to contribute and share your story? You can submit here - patientworthy.com/contribute/ - OR let us know if you'd like to work with a writer.

Regulatory Fast-Track Transforms Lung Cancer Treatment Timeline; Gene Therapy Withdrawal Signals Market Challenges bit.ly/4s5bq6h Read now at PatientWorthy.com #PatientWorthy #LungCancer #GeneTherapy

Japan Advances Targeted Breast Cancer Treatment: Daiichi Sankyo Seeks Approval for Innovative Therapy After Surgery bit.ly/4rvcrDU Read now at PatientWorthy.com #PatientWorthy #BreastCancer #HER2PositiveBreastCancer #Enhertu

Scientists Redesign HIV-Fighting Antibodies to Strike Faster: A New Engineering Breakthrough bit.ly/46Tz3X7 Read now at PatientWorthy.com #PatientWorthy #HIV

Amber #amberrrrjaned1990 a loving mother and advocate for her son who is living with Duchenne muscular dystrophy (DMD). “It is important for kids to have friends with similar disabilities, so they know they are not alone.”#DMD #shareyourstory #patientworthy #caregivers

Momentum Builds Across Biotech Pipeline: Seizure Breakthrough, Cell Therapy Revival, and Obesity Medicine Gains bit.ly/4uvdTZG Read now at PatientWorthy.com #PatientWorthy #Seizure #CellTherapy #Obesity

Study: Engineered Immune Cells and Targeted Treatments May Slow the Spread of Triple-Negative Breast Cancer bit.ly/40q55X8 Read now at PatientWorthy.com #PatientWorthy #BreastCancer #Triple-NegativeBreastCancer

Breakthrough DNA Repair Inhibitor Advances Rapidly Toward Clinic: Artios' ART6043 Earns FDA Fast Track Status for Resistant Breast Cancer bit.ly/4btK5UC Read now at PatientWorthy.com #PatientWorthy #BreastCancer #ArtiosPharma #ART6043 #FDAFastTrackStatus

Daiichi Sankyo Advances Enhertu for High-Risk Breast Cancer: New Hope After Neoadjuvant Therapy bit.ly/4rM3VB4 Read now at PatientWorhty.com #PatientWorthy #Enhertu #BreastCancer #HER2+BreastCancer

The FDA Has approved Bristol Myers Squibb's new medication Sotyktu for the treatment of psoriatic arthritis. Read more here: patientworthy.com/2026/03/12/fda…

Patient Worthy is honored to share this caregiver story from our friends at the Courageous Parents Network, written by Aisling Melton about her daughter Éabha's fight against brain cancer. Read here: patientworthy.com/2026/03/12/lea…

Accelerated Pathway Opens for GSK's Pruritus Solution in China's Rare Liver Disease Population bit.ly/408bCpe Read now at PatientWorthy.com #PatientWorthy #RareLiverDisease #PrimaryBiliaryCholangitis #PBC

Two Intellia Clinical Trials Released by the FDA bit.ly/4rOa6oh Read now at PatientWorthy.com #PatientWorthy #ATTR #Amyloidosis #FDAApproval

Gene Therapy Setback: REGENXBIO's RGX-121 Faces Regulatory Hurdles in Ultra-Rare Disease Treatment bit.ly/4b12esi Read now at PatientWorthy.com #PatientWorthy #MPSII #HunterSyndrome #REGENXBIO #RGX-121

New research may offer hope for people living with #PKU. While still in development, this approach reflects growing momentum toward potentially durable, one-time genetic treatments for rare diseases. patientworthy.com/2026/03/10/new…

From Psychiatric Bind to Clinical Solution: The VMAT2 Revolution in Treating Tardive Dyskinesia bit.ly/407UiRa Read now at PatientWorthy.com #PatientWorthy #VMAT2 #TardiveDyskinesia

Brain Cancers: FDA Approves Pembrolizumab Combo bit.ly/4aZuXxS Read now at PatientWorthy.com #PatientWorthy #BrainCancer #Penbrolizumab #Glioblastoma #Astrocytoma

Breaking New Ground: Milsaperidone Offers Patients a Fresh Option for Serious Mental Illness bit.ly/4aMibUD Read now at PatientWorthy.com #PatientWorthy #MentalIllness #Schizophrenia #Bipolar1 #Milsaperidone

We had the pleasure of meeting Krista at Rare Disease Week on Capitol Hill! Krista was diagnosed with Usher syndrome. #RareDC2026 #PatientWorthy #RareArtist

Breaking New Ground: FDA Green-Lights Novel Breast Cancer Treatment Targeting Treatment-Resistant Tumors bit.ly/4avaWQM Read now at PatientWorthy.com #PatientWorthy #BreastCancerTreatment #ClinicalTrial #Giredestrant

FDA Approves Revolutionary Oral Combination Therapy for Chronic Lymphocytic Leukemia, Offering Patients Freedom from Long-Term Treatment bit.ly/4qYAbQp Read now at PatientWorthy.com #PatientWorthy #ChronicLymphocyticLymphoma #CLL