
On #RareDiseaseDay & every day, we leverage AI to repurpose drugs to treat #RareDiseases like TTR Amyloidosis, Phenylketonuria, Tardive Dyskinesia or Duchenne Muscular Dystrophy.
ℹWe’re carrying out a Phase 2b clinical trial to treat Chorea in Huntington’s Disease. #CareForRare

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