Sabitlenmiş Tweet
SpliceBio
199 posts

SpliceBio
@SpliceBioHQ
Genetic medicines company harnessing Protein Splicing to develop the next-gen of gene therapies. Based on technology developed in the Muir Lab at @Princeton.
Barcelona Katılım Şubat 2018
56 Takip Edilen313 Takipçiler

#Stargardt disease has no approved treatments. This #HealthyVisionMonth, we’re raising awareness of inherited retinal diseases. At SpliceBio, we’re working to advance genetic medicines using protein splicing to address diseases caused by mutations in large genes.

English

We’re heading to #ASGCT2026 next week! Looking forward to connecting with the community, sharing insights, and contributing to the conversation around #genetherapy at the @ASGCTherapy Annual Meeting. See you there!

English

Great science starts with great people. Today, we celebrate the SpliceBio team whose passion and collaboration power our work in genetic medicines. Thank you for all you do. Happy #InternationalWorkersDay!
English

Happy #SantJordi and #WorldBookDay 🌹📖
Today, we’re celebrating a Catalan tradition of books, roses and storytelling with our team in Barcelona. Here’s to a day of love and culture, with roses for all!
English

Feliç #SantJordi i #WorldBookDay 🌹📖Avui celebrem una tradició catalana de llibres, roses i històries amb el nostre equip a Barcelona. Un dia per celebrar l’amor i la cultura, amb roses per a tothom!




Català

Our CMO Aniz Girach will present at the Annual Retinal Therapeutics Innovation Summit in Denver, co-hosted by @FightBlindness and @CaseyEye. He’ll share the progress of our clinical program SB-007, a third-generation intein-based dual AAV in development for Stargardt disease.

English

Our co-founder and CEO sat down with @CheckRare to discuss SB-007, our investigational dual-AAV gene therapy for #Stargardt disease, and how it is designed to enable delivery of the full-length ABCA4 protein.
English

For #RareDiseaseDay, we came together to name our newest plush teammate, “Tira,” inspired by a zebra in Kenya born with a rare genetic condition that altered her stripe pattern.🦓Tira is a reminder of why we do this work and who we do it for.



English

We have a fierce appreciation for women in STEM! On International Day of Women and Girls in Science, we recognize all of the incredible women at SpliceBio who are transforming the future of genetic medicines and are paving the way for future generations. #WomeninSTEM




English

Listen to the full episode on The BioHub Podcast.⬇️
Spotify: lnkd.in/e-6YHEBk
Apple: lnkd.in/eyt85Zpx
English

#Stargardt disease is a condition that leads to central vision loss & blindness. Caused by biallelic mutations in the ABCA4 gene, it remains a significant unmet need with no approved treatments. This #LowVisionAwarenessMonth, learn how SB-007 targets the underlying genetic cause.
English

We are pleased to announce that the first patient has been dosed in the Part B dose expansion portion of our Phase 1/2 ASTRA clinical trial of SB-007, a dual adeno-associated viral vector gene therapy for the treatment of #Stargardt disease.

English




