Mary Fiance

Proud to receive this recognition from @marquiswhoswho for my work in #communications 🎉 24-7pressrelease.com/press-release/…

Click the link below to donate and support MDA efforts to find treatments bit.ly/BrookeALS #MDAPartner #EndALSwithMDA #EndALS #ALS @MDAorg

MDA 2026 keynote speaker John Crowley discussed with MD News Today the progress made in neuromuscular disease and the future challenges. buff.ly/7Gn3wrQ #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Consuming more dietary protein may benefit people with various types of muscular dystrophy, according to a recent study. buff.ly/yEyCKdm #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

PGN-EDODM1, an experimental DM1 therapy from Pepgen, showed biomarker activity and splicing correction in an early clinical trial. buff.ly/qt0AJSZ #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

New presentations at MDA 2026 expand the understanding of how Duvyzat may help people with Duchenne muscular dystrophy. buff.ly/o9eztsF #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Dyne Therapeutics' Z-basivarsen led to gains in motor function and cognition for myotonic dystrophy type 1, and is entering a Phase 3 trial. musculardystrophynews.com/news/mda-2026-… #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Capricor has reapplied for FDA approval of deramiocel, its therapy for DMD-related heart disease, and expects a decision by August 22. buff.ly/vJbEqLB #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

The evidence for Elevidys is growing, and Sarepta is working to make the DMD treatment widely available, the company's research president said. buff.ly/7asZgkB #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

Dyne Therapeutics is advancing z-rostudirsen toward approval for DMD after data showed increased dystrophin and early functional trends. buff.ly/2XCPFsk #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

The MDA's annual conference highlighted recent breakthroughs and the outlook for future care in the neuromuscular disease community. buff.ly/utBSY3y #musculardystrophynews #musculardystrophy #musculardystrophycommunity #livingwithMD

We've resubmitted our BLA to the FDA for our investigational, muscle-targeted treatment for SMA! Our progress reaffirms the promise of myostatin biology as we continue to prioritize scientific advancement & the needs of children & adults living with SMA. bit.ly/4sIxX9x

📢 Big news for the SMA community: The FDA has approved a high-dose SPINRAZA regimen for SMA—another major step forward in care. Developed by @biogen, this milestone builds on decades of MDA-supported research. Progress keeps moving 🔗 mda.org/press-releases… #SMA #Research

#News: Today, the FDA approved a new dosing regimen option for our spinal muscular atrophy (SMA) therapy. This approval represents an important step toward expanding options for people living with SMA. Learn more: ow.ly/94tg50YAA9p

#News: At the 2026 #MDAConference, hosted by @MDAorg, we’re presenting new Phase 1b results and details on the Phase 3 clinical development program for an investigational spinal muscular atrophy (SMA) medicine. Read more: ow.ly/g07g50YshGO

#MDAConference: Sharon Hesterlee, MD, president and CEO of the Muscular Dystrophy Association, opening the @MDAorg’s 2026 Clinical & Scientific Conference in Orlando, FL. #RareDisease #MuscularDystrophy #MedTwitter

#MDAConference: Lily Sander, 18, @MDAorg's 2026 National Ambassador, who introduced Allison Moore, founder and CEO of the Hereditary Neuropathy Foundation, and winner of the 2026 MDA Legacy Award for Achievement in Clinical Research. #RareDisease #CharcotMarieToothDisease

#MDAConference: Łukasz J Sznajder, PhD, an assistant professor at the @unlv, and winner of the 2026 @MDAorg Research Momentum Award Image & quote taken by Senior Correspondent, @LLuxner. #RareDisease #MuscularDystrophy

#MDAConference: Allison Moore, winner of the 2026 @MDAorg Donavon Decker Community Impact in Research Award. Moore, who has Charcot-Marie-Tooth disease, is founder and CEO of the Hereditary Neuropathy Foundation. #RareDisease #MuscularDystrophy #CharcotMarieToothDisease

#MDAConference: Susan Apkon, MD, pediatric neurologist at @ChildrensColo speaking March 9 about #Duchenne muscular dystrophy at the 2026 @MDAorg Clinical & Scientific Conference in Orlando, FL. Image & quote by Senior Correspondent, @LLuxner. #RareDisease #MuscularDystrophy

#MDAConference: John Crowley, father of two kids with #Pompe and former CEO of @amicusrx1. Crowley, now president and CEO of the @IAmBiotech, spoke March 9 at the @MDAorg's 2026 Clinical & Scientific Conference in Orlando, FL. #RareDisease #MuscularDystrophy #PompeDisease