SMA Research

Today is #UKSMAAwarenessDay! Spinal Muscular Atrophy is a rare, genetically inherited neuromuscular condition. Please retweet to help raise awareness of #SMA

UK #SMA Research conference attendees, representing @NDCNOxford @EdinUniNeuro @neuroshef SMAReach @UCL_ICH @ryanezmunoz @ISTM_Keele @univofstandrews - Mostly all funded by @smatrust at some point!

A day at #SITRAN, finding out what the UK #SMA laboratories are working on. Keynote delivered by Prof Azzouz on DNA damage in SMA.

End-of-study results from Biogen's CHERISH trial demonstrate stabilisation or improvement in motor function in individuals with #SMA, where the natural history of the disease is a decline in motor function over time. bit.ly/2HPjJh0

#SMAEurope held its first international scientific congress on #SMA in Krakow, Poland 🎓. It was a huge success. Find out more from @drgroen : bit.ly/2sHBSts

Scottish Medicines Consortium will be assessing #nusinersen for patients with SMA. We will be working with @SMASupportUK & @smatrust to provide a Patient Group Submission. #SMA

RT @amrc: Please read our statement on the Government's announcement of a new accelerated access pathway: bit.ly/2yrog8o #sma

RT @SMAEurope: 2 days left before abstract submisson deadline 4 our int. scientific Congress on #SMA. Get them in! ow.ly/Nh3A30g7NbQ

Roche provided a community statement on the SUNFISH clinical trial RG7916 for #SMA. Find out what it says here: ow.ly/Id3a30fVMoq

Can you help? twitter.com/ryanezmunoz/st…

We expect an exiting meeting with top invited speakers, oral presentations from selected abstracts, posters, workshops, prizes. Do not miss! twitter.com/SMAEurope/stat…

AveXis 2 initiate pivotal trial for gene replacement product, AVXS-101, in #SMA Type 1 in the U.S. ow.ly/hGFc30fBnc4

Roche announces start of the 2nd part of the Phase 2 #SUNFISH clinical trials 4 Type 2/3 #SMA. Find out more: ow.ly/4Kgo30fenjT

NHS England to fund hospital costs of administering #Spinraza 4 patients with #SMA Type 1 on Biogen’s EAP. ow.ly/Roi630eaCrW

SRK-015, a potential new #SMA therapy by Scholar Rock, 2 enter clinical trials soon, based on encouraging data: ow.ly/wjlC30dty3e

Biogen provides a summary of discussion between @SMAEurope & Biogen reps on EU list price for #nusinersen. #sma bit.ly/2tLLsuX

All Party Parliamentary Group to discuss access to #nusinersen in the UK at the Houses of Parliament #sma #spinraza: bit.ly/2tLuJIa

Read our update from an NHS England meeting on the SMA Type 1 Expanded Access Programme 4 #nusinersen #spinraza #sma bit.ly/2uNeNln

New #SMA research grants awarded by @SMAEurope following recommendations by its Scientific Advisory Board. Find out: ow.ly/i5rN30dhilr