Richard Voit

217 posts

Richard Voit

Richard Voit

@RichardVoit

Pediatric hematology/oncology | Stem cell biology | AML | Gene therapy | CRISPR

UT Southwestern Katılım Aralık 2021
193 Takip Edilen326 Takipçiler
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Richard Voit
Richard Voit@RichardVoit·
Gene therapy is transforming how we treat genetic disorders, but what if mutations in more than 30 genes can cause similar symptoms? Now published in @CellStemCell (cell.com/cell-stem-cell…), we report the development of a universal gene therapy for Diamond Blackfan anemia. 1/n
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Richard Voit
Richard Voit@RichardVoit·
Congrats Walter! Trainees and folks looking for a new and exciting challenge: don’t pass up this opportunity to work with Walter!
Walter W. Chen, MD, PhD@WalterWChen1

Thrilled to share that I’ll be starting my lab as an Assistant Professor and Endowed Scholar in @UTSWMedCenter Molecular Biology Dept this Fall! 🥳 We’ll study #peroxisomes #mitochondria #metabolism via the lens of neonatology👶🏻, a very exciting frontier in medicine! #neotwitter

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Vijay Sankaran
Vijay Sankaran@bloodgenes·
❓A one-time, durable, and even reversible way to prevent thrombosis? In this preprint, led by @lrbzldz, we show that epigenome editing of 🩸 #StemCells can durably reprogram platelet function: biorxiv.org/content/10.648…
Vijay Sankaran tweet media
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Sean
Sean@S_Gallagher23·
FDA just approved Kresladi (marnetegragene autotemcel) for severe LAD-I — a disease so rare there are ~25 new cases a year in the U.S. The pivotal data: 9 patients. 100% overall survival. All endpoints met. This approval is a masterclass in how to think about evidence standards when mechanism is unambiguous. fda.gov/news-events/pr…
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Daniel Bauer
Daniel Bauer@danielevanbauer·
In this piece, my mentor Stu Orkin and I (1) marvel at prime editing—discovery to disease correction for 2 patients after just 6 yr—wow Liu, Anzalone, Gori, Malech et al! & (2) consider the challenges to deliver genetic medicine’s promise for 2^n patients nejm.org/doi/full/10.10…
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The V Foundation for Cancer Research
The V Foundation for Cancer Research@TheVFoundation·
We fund researchers like @kennethschen, one of the brilliant minds that is helping to shape the future of cancer research. V Foundation researchers, throughout their careers, have generated $22 billion in additional cancer research funding. We truly fund the best of the best.
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Elvin Wagenblast
Elvin Wagenblast@Elvin_Wag·
Be part of the Wagenblast Lab! We are hiring a Lab Manager for leukemia & blood stem cell research at @IcahnMountSinai in NYC, starting July 2025. See ad to apply!
Elvin Wagenblast tweet media
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Richard Voit
Richard Voit@RichardVoit·
Kids like KK motivate everything we do in the lab @utswcancer @CRI_UTSW @UTSW_PedsHemOnc. We are now hiring so if you are looking for the next step in your scientific journey or want to learn more about what we do, please reach out.
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Keşfet

@lrbzldz @kennethschen @tjflemin @Mendell_lab @JaviGBermudez @HijaiShin @pewtrusts @UTSWScience