Christopher Heier

Happy to share our latest article: Deletion of miR-146a enhances therapeutic protein restoration in model of dystrophin exon skipping: Molecular Therapy - Nucleic Acids cell.com/molecular-ther…. Congrats to first author and talented post-doc @nikkimmccormack! #DMD #microRNA (1/3)

Our new paper is published! Learning more about how steroids work in #Duchenne. Congrats to Trinitee on her first 1st author paper! @DMM_Journal has a nice interview with her, link to follow. @MDAorg @ParentProjectMD @FiorilloLab @MYOTWlTTER #DMD journals.biologists.com/dmm/article-lo…

The recent @fda approval of the #MDA-Supported Drug AGAMREE® (vamorolone) from @catalystforrare is a beacon of hope for people living with #Duchenne #MuscularDystrophy (#DMD), a rare but serious degenerative muscle disease. Learn more in #Quest: mdaquest.org/agamree-vamoro…

“CureDuchenne is proud to have contributed to the early development of vamorolone at ReveraGen." cureduchenne.org/general/fda-ap…

#MDA celebrates the @US_FDA approval of AGAMREE® (vamorolone) to treat children and adolescents living with #Duchenne #MuscularDystrophy (#DMD). Learn more about this novel therapy, supported in part by MDA Venture Philanthropy: mda.org/press-releases…

Today, the U.S. Food and Drug Administration (FDA) has granted its approval for Vamorolone, a new treatment for Duchenne Muscular Dystrophy (DMD) aged 2 years and older. worldduchenne.org/news/fda-appro…

EMA's CHMP issued a positive opinion in favor of the approval of AGAMREE® (vamorolone) for DMD patients aged 4 years and up. 🤝 The Duchenne community's contributions as funders, research participants, and our support as @Vision_DMD partner were pivotal. worldduchenne.org/news/europe-ch…

PhD Opportunity #Myotwitter If you are interested in the mechanisms regulating skeletal muscle adaptability then please apply to join my new lab @UCNZ, Christchurch, New Zealand! tinyurl.com/SMUcP Scholarships are available for stipend + tuition fees. Please RT

Positive news for boys with #Becker #MuscularDystrophy: Vamorolone improves disease progression with fewer side effects than current treatments. Read more from @TheHeierLab, @AlysonAFiorillo & the Center for Genetic Medicine Research. ⬇️ …ovationdistrict.childrensnational.org/new-becker-mus…

Our new paper is out! Vamorolone improves disease and increases dystrophin in our Becker muscular dystrophy model. Now in clinical trials (NCT05166109) #bmd #Becker #dystrophin #myotwitter @FiorilloLab @TheHeierLab @MYOTWlTTER cell.com/iscience/fullt…

@CBKReport Greg Ostertag, when he ran over his own foot with a van

When you see this logo, what’s the first player/moment you think of?

Great time at #MDAconference in Dallas, Texas, sharing my recent work on TPM3-related myopathy. 🧑‍🔬🦓💪 #RareDiseases #Muscle #Science #Myotwitter @BostonChildrens @harvardmed @MDAorg

Great to see @MatthiasLambert @AlysonAFiorillo @HogarthMarshall and other next generation muscle disease research leaders feature in Genetic mechanisms session at #MDA2023 @MDAorg

It was a pleasure working with co-editors @RikaMaruyama_E, @AlysonAFiorillo, @MacGyver0282, and Dongsheng Duan. Looking forward to more breakthroughs in the field! #ScienceAdvances #NeuroMuscularDiseases

@TheFFBallers 🫴

Reply with a 🫴 and we'll give you a very generic customized fantasy team name

Attending @GordonConf Seminar as invited plenary speaker and extremely disappointed that Handicap ppl are STILL not considered eligible for the Carl Storm travel fellowship even after the big fight I had in 2018. I guess I don’t quite understand what the word minority means 🤷🤷

Tom Brady and Tony Dungy looking like they poisoned your food and are waiting for you to eat it

1st mouse model of Becker muscular dystrophy!! Excited our bmx paper came out this week, check it out here: #Beckermusculardystrophy @AlysonAFiorillo @FiorilloLab @nikkimmccormack @EdgewiseTx @MDAorg @CureBMD @MDUK_News @ParentProjectMD #dystrophin onlinelibrary.wiley.com/doi/10.1002/jc…

Investigators at the Center for Genetic Medicine Research @AlysonAFiorillo & @MacGyver0282 created a model to test new treatments for Becker muscular dystrophy, providing hope to the growing number of patients with this debilitating neuromuscular disease. spr.ly/60173pSMX